16:00 to 17:00
Lecture

From pathophysiology to treatment of monogenic diseases (1)

Jean-Louis Mandel
Salle 2, Site Marcelin Berthelot
Open to all, subject to availability
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Introduction: some "classic" successes in the treatment of genetic diseases, and some unforeseen problems (Phenylketonuria, Hemophilia A, Enzyme replacement therapies...).